Description
This panel contains genes associated with hypophosphataemia or rickets. 

It has been compared against the Genomics England PanelApp 'hypophosphataemia or rickets' panel V4.1, with all discrepancies reviewed and resolved (October 2025).

5 reviewers

  • Teresa Zhao (Victorian Clinical Genetics Services)

  • Chirag Patel (Genetic Health Queensland)

  • Bryony Thompson (Royal Melbourne Hospital)

  • Zornitza Stark (Victorian Clinical Genetics Services)

  • Krithika Murali (Victorian Clinical Genetics Services)

19 Entities

19 reviewed, 15 green

List Entity Reviews Mode of inheritance Details
19 Entitiess
Green Green List (high evidence)
ALPL
1 review
1 green
BIALLELIC, autosomal or pseudoautosomal
Sources
  • Expert Review Green
  • Victorian Clinical Genetics Services
Phenotypes
  • Hypophosphatasia, infantile, MIM# 241500
Tags
  • treatable
Green Green List (high evidence)
CLCN5
2 reviews
1 green
X-LINKED: hemizygous mutation in males, biallelic mutations in females
Sources
  • Expert Review Green
  • Victorian Clinical Genetics Services
Phenotypes
  • Hypophosphatemic rickets, MIM# 300554
Tags
Green Green List (high evidence)
CTNS
1 review
1 green
BIALLELIC, autosomal or pseudoautosomal
Sources
  • Expert list
  • Expert Review Green
Phenotypes
  • Cystinosis, nephropathic MIM#219800
Tags
  • treatable
Green Green List (high evidence)
CYP27B1
1 review
BIALLELIC, autosomal or pseudoautosomal
Sources
  • Expert List
  • Expert Review Green
Phenotypes
  • Vitamin D-dependent rickets, type I MIM#264700
Tags
  • treatable
Green Green List (high evidence)
CYP2R1
1 review
1 green
BIALLELIC, autosomal or pseudoautosomal
Sources
  • Expert list
  • Expert Review Green
Phenotypes
  • Rickets due to defect in vitamin D 25-hydroxylation MIM#600081
Tags
Green Green List (high evidence)
DMP1
1 review
1 green
BIALLELIC, autosomal or pseudoautosomal
Sources
  • Expert List
  • Expert Review Green
Phenotypes
  • Hypophosphatemic rickets MIM#241520
Tags
Green Green List (high evidence)
ENPP1
1 review
1 green
BIALLELIC, autosomal or pseudoautosomal
Sources
  • Expert Review Green
  • Victorian Clinical Genetics Services
Phenotypes
  • Hypophosphatemic rickets, autosomal recessive, 2, MIM# 613312
Tags
Green Green List (high evidence)
FAH
1 review
1 green
BIALLELIC, autosomal or pseudoautosomal
Sources
  • Expert Review Green
  • Victorian Clinical Genetics Services
Phenotypes
  • Tyrosinemia, type I, MIM# 276700
Tags
  • treatable
Green Green List (high evidence)
FAM20C
1 review
1 green
BIALLELIC, autosomal or pseudoautosomal
Sources
  • Expert list
  • Expert Review Green
Phenotypes
  • Raine syndrome, MIM# 259775
Tags
Green Green List (high evidence)
FGF23
1 review
1 green
MONOALLELIC, autosomal or pseudoautosomal, NOT imprinted
Sources
  • Expert List
  • Expert Review Green
Phenotypes
  • Autosomal dominant hypophosphatemic rickets MONDO:0008660
Tags
Green Green List (high evidence)
OCRL
1 review
1 green
X-LINKED: hemizygous mutation in males, biallelic mutations in females
Sources
  • Expert Review Green
  • Victorian Clinical Genetics Services
Phenotypes
  • Lowe syndrome, MIM# 309000
Tags
Green Green List (high evidence)
PHEX
2 reviews
2 green
X-LINKED: hemizygous mutation in males, monoallelic mutations in females may cause disease (may be less severe, later onset than males)
Sources
  • Expert Review Green
  • KidGen_CalcPhos v38.1.0
  • Victorian Clinical Genetics Services
Phenotypes
  • Hypophosphatemic rickets, MIM#307800
Tags
  • SV/CNV
Green Green List (high evidence)
SLC34A1
1 review
1 green
BOTH monoallelic and biallelic, autosomal or pseudoautosomal
Sources
  • Expert List
  • Expert Review Green
Phenotypes
  • Nephrolithiasis/osteoporosis, hypophosphatemic, 1, MIM#612286
Tags
Green Green List (high evidence)
SLC34A3
1 review
1 green
BIALLELIC, autosomal or pseudoautosomal
Sources
  • Expert Review Green
  • Victorian Clinical Genetics Services
Phenotypes
  • Hypophosphataemic rickets with hypercalciuria, (MIM#241530)
Tags
Green Green List (high evidence)
VDR
1 review
1 green
BIALLELIC, autosomal or pseudoautosomal
Sources
  • Expert List
  • Expert Review Green
Phenotypes
  • Rickets, vitamin D-resistant, type IIA, MIM# 277440
Tags
Amber Amber List (moderate evidence)
CYP3A4
1 review
MONOALLELIC, autosomal or pseudoautosomal, NOT imprinted
Sources
  • Expert Review
  • Expert Review Amber
Phenotypes
  • Vitamin D-dependent rickets, type 3, MIM#619073
Tags
Amber Amber List (moderate evidence)
KL
1 review
Unknown
Sources
  • Expert Review Amber
  • Victorian Clinical Genetics Services
Tags
Red Red List (low evidence)
SGK3
2 reviews
2 red
MONOALLELIC, autosomal or pseudoautosomal, NOT imprinted
Sources
  • Expert Review Red
  • Literature
Phenotypes
  • Hypophosphatemic rickets
Tags
Red Red List (low evidence)
SLC9A3R1
1 review
1 red
MONOALLELIC, autosomal or pseudoautosomal, NOT imprinted
Sources
  • Expert Review Red
  • KidGen_CalcPhos v38.1.0
Phenotypes
  • Nephrolithiasis/osteoporosis, hypophosphatemic, 2, MIM# 612287
Tags

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