Description
UNDER CONSTRUCTION. DO NOT USE.

6 reviewers

  • Lilian Downie (Victorian Clinical Genetics Services)

  • Zornitza Stark (Victorian Clinical Genetics Services)

  • David Eckstein (Other)

  • Abigail Veldman (Other)

  • Katrina Stone (Other)

  • Judit Garcia (Other)

11 Entities

10 reviewed, 5 green

List Entity Reviews Mode of inheritance Details
11 Entitiess
Green Green List (high evidence)
ACADM
1 review
1 green
BIALLELIC, autosomal or pseudoautosomal
Sources
  • Expert list
  • Expert Review Green
Phenotypes
  • Acyl-CoA dehydrogenase, medium chain, deficiency of MIM# 201450
Tags
Green Green List (high evidence)
ALDH7A1
2 reviews
2 green
BIALLELIC, autosomal or pseudoautosomal
Sources
  • Expert Review Green
  • Other
Phenotypes
  • Epilepsy, pyridoxine-dependent, MIM#266100
Tags
Green Green List (high evidence)
CBS
2 reviews
1 green
BIALLELIC, autosomal or pseudoautosomal
Sources
  • Expert list
  • Expert Review Green
Phenotypes
  • Homocystinuria, B6-responsive and nonresponsive types MIM#236200
Tags
Green Green List (high evidence)
GAMT
2 reviews
2 green
BIALLELIC, autosomal or pseudoautosomal
Sources
  • Expert Review
  • Expert Review Green
Phenotypes
  • Creberal creatine deficiency syndrome 2 (MIM 612736)
Tags
Green Green List (high evidence)
TCN2
2 reviews
1 green
BIALLELIC, autosomal or pseudoautosomal
Sources
  • Expert list
  • Expert Review Green
Phenotypes
  • Transcobalamin II deficiency, MIM#275350
Tags
Amber Amber List (moderate evidence)
ABCC8
2 reviews
1 green
MONOALLELIC, autosomal or pseudoautosomal, NOT imprinted
Sources
  • Expert list
  • Expert Review Amber
Phenotypes
  • Diabetes mellitus, permanent neonatal 3 MIM# 618857
Tags
Red Red List (low evidence)
ACADVL
1 review
1 green
BIALLELIC, autosomal or pseudoautosomal
Sources
  • Expert list
Phenotypes
  • VLCAD deficiency MIM#201475
Tags
Red Red List (low evidence)
AK2
1 review
BIALLELIC, autosomal or pseudoautosomal
Sources
  • Expert list
Tags
Red Red List (low evidence)
PAH
1 review
1 green
BIALLELIC, autosomal or pseudoautosomal
Sources
  • Expert list
Phenotypes
  • Phenylketonuria MIM#261600
Tags
No list No list
F9
0 reviews
X-LINKED: hemizygous mutation in males, monoallelic mutations in females may cause disease (may be less severe, later onset than males)
Sources
  • Expert list
Phenotypes
  • Hemophilia B
Tags
No list No list
GLA
1 review
X-LINKED: hemizygous mutation in males, monoallelic mutations in females may cause disease (may be less severe, later onset than males)
Sources
  • ClinGen
  • Literature
Phenotypes
  • Fabry disease (MIM 301500)
  • Fabry disease, cardiac variant (MIM 301500)
Tags

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