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Mendeliome v1.4525 ASCL5 Zornitza Stark Marked gene: ASCL5 as ready
Mendeliome v1.4525 ASCL5 Zornitza Stark Gene: ascl5 has been classified as Amber List (Moderate Evidence).
Mendeliome v1.4525 ASCL5 Zornitza Stark Classified gene: ASCL5 as Amber List (moderate evidence)
Mendeliome v1.4525 ASCL5 Zornitza Stark Gene: ascl5 has been classified as Amber List (Moderate Evidence).
Mendeliome v1.4524 ASCL5 Zornitza Stark gene: ASCL5 was added
gene: ASCL5 was added to Mendeliome. Sources: Literature
founder tags were added to gene: ASCL5.
Mode of inheritance for gene: ASCL5 was set to MONOALLELIC, autosomal or pseudoautosomal, NOT imprinted
Publications for gene: ASCL5 were set to 41673016
Phenotypes for gene: ASCL5 were set to Tooth disorder, MONDO:0006999, ASCL5-related
Review for gene: ASCL5 was set to AMBER
Added comment: [PMID 41673016] reports 17 individuals from 6 unrelated families with heterozygous missense ASCL5 c.274G>A (p.Glu92Lys) variants presenting with autosomal‑dominant lobodontia, characterized by supernumerary cusps, single pyramidal roots, and taurodontism. The variant fully co‑segregates with disease, is absent from population databases, and functional studies (CRISPR knock‑in mouse, luciferase reporter, RNA‑seq) demonstrate loss‑of‑function of ASCL5 transcriptional activation.

Amber rating due to this being a likely founder variant and not necessarily perceived as disease.
Sources: Literature