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Progressive Myoclonic Epilepsy v0.26 CLN5 Zornitza Stark Marked gene: CLN5 as ready
Progressive Myoclonic Epilepsy v0.26 CLN5 Zornitza Stark Gene: cln5 has been classified as Green List (High Evidence).
Progressive Myoclonic Epilepsy v0.26 CLN5 Zornitza Stark Publications for gene: CLN5 were set to
Progressive Myoclonic Epilepsy v0.25 CLN5 Zornitza Stark reviewed gene: CLN5: Rating: GREEN; Mode of pathogenicity: None; Publications: ; Phenotypes: Ceroid lipofuscinosis, neuronal, 5, MIM# 256731; Mode of inheritance: BIALLELIC, autosomal or pseudoautosomal
Progressive Myoclonic Epilepsy v0.22 CLN5 Noor Al-Ali reviewed gene: CLN5: Rating: GREEN; Mode of pathogenicity: Loss-of-function variants (as defined in pop up message) DO NOT cause this phenotype - please provide details in the comments; Publications: (PMID: 20157158, 41003830, 39667065, 22532218, 32983231); Phenotypes: Onset at 4 to 7 years, progressive vision loss, retinal degeneration, nystagmus, clumsiness, motor deterioration, developmental regression, ataxia, dysarthria, dysmetria, dysdiadochokinesis, seizures, myoclonus, intellectual disability, cognitive impairment, neurophysiologic abnormalities (EEG, VEP, SEP), characteristic findings on MRI, autofluorescent lipopigment in neurons, cerebellar atrophy (in one family), concentration difficulties, “fingerprint” profiles ultrastructurally, “curvilinear” profiles ultrastructurally, “rectilinear” profiles ultrastructurally.; Mode of inheritance: BIALLELIC, autosomal or pseudoautosomal
Progressive Myoclonic Epilepsy v0.22 CLN5 Noor Al-Ali Deleted their review
Progressive Myoclonic Epilepsy v0.22 CLN5 Noor Al-Ali reviewed gene: CLN5: Rating: GREEN; Mode of pathogenicity: Loss-of-function variants (as defined in pop up message) DO NOT cause this phenotype - please provide details in the comments; Publications: (PMID: 20157158, 41003830, 39667065, 22532218, 32983231); Phenotypes: Onset at 4 to 7 years, progressive vision loss, retinal degeneration, nystagmus, clumsiness, motor deterioration, developmental regression, ataxia, dysarthria, dysmetria, dysdiadochokinesis, seizures, myoclonus, intellectual disability, cognitive impairment, neurophysiologic abnormalities (EEG, VEP, SEP), characteristic findings on MRI, autofluorescent lipopigment in neurons, cerebellar atrophy (in one family), concentration difficulties, “fingerprint” profiles ultrastructurally, “curvilinear” profiles ultrastructurally, “rectilinear” profiles ultrastructurally; Mode of inheritance: MONOALLELIC, autosomal or pseudoautosomal, NOT imprinted
Progressive Myoclonic Epilepsy v0.0 CLN5 Bryony Thompson gene: CLN5 was added
gene: CLN5 was added to Progressive Myoclonic Epilepsy_RMH. Sources: Expert Review Green,Royal Melbourne Hospital
Mode of inheritance for gene: CLN5 was set to BIALLELIC, autosomal or pseudoautosomal
Phenotypes for gene: CLN5 were set to Ceroid lipofuscinosis, neuronal, 5, MIM#256731