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Progressive Myoclonic Epilepsy v0.22 CTSF Noor Al-Ali reviewed gene: CTSF: Rating: RED; Mode of pathogenicity: Loss-of-function variants (as defined in pop up message) DO NOT cause this phenotype - please provide details in the comments; Publications: No publications showing an association between pathogenic variants of the CTSF gene and progressive myoclonic epilepsy (PME); Phenotypes: : Progressive cognitive decline, dementia, motor abnormalities, tremor, ataxia, dysarthria, cerebellar signs, extrapyramidal signs, myoclonus, perioral dyskinesias, hyperreflexia, extensor plantar responses, primitive reflexes, seizures, diffuse cerebral atrophy, cerebellar atrophy, accumulation of autofluorescent material in neurons, behavioral changes, emotional lability, depression, skin fibroblasts showing osmiophilic cytoplasmic inclusions.; Mode of inheritance: BIALLELIC, autosomal or pseudoautosomal
Progressive Myoclonic Epilepsy v0.0 CTSF Bryony Thompson gene: CTSF was added
gene: CTSF was added to Progressive Myoclonic Epilepsy_RMH. Sources: Expert Review Green,Royal Melbourne Hospital
Mode of inheritance for gene: CTSF was set to BIALLELIC, autosomal or pseudoautosomal
Phenotypes for gene: CTSF were set to Ceroid lipofuscinosis, neuronal, 13, Kufs type, 615362