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Mendeliome v2.502 DCTN4 Rylee Peters Marked gene: DCTN4 as ready
Mendeliome v2.502 DCTN4 Rylee Peters Gene: dctn4 has been classified as Amber List (Moderate Evidence).
Mendeliome v2.502 DCTN4 Rylee Peters Classified gene: DCTN4 as Amber List (moderate evidence)
Mendeliome v2.502 DCTN4 Rylee Peters Gene: dctn4 has been classified as Amber List (Moderate Evidence).
Mendeliome v2.501 DCTN4 Rylee Peters gene: DCTN4 was added
gene: DCTN4 was added to Mendeliome. Sources: Literature
Mode of inheritance for gene: DCTN4 was set to MONOALLELIC, autosomal or pseudoautosomal, NOT imprinted
Publications for gene: DCTN4 were set to 42378292
Phenotypes for gene: DCTN4 were set to Neurodevelopmental disorder, MONDO:0700092, DCTN4-related
Review for gene: DCTN4 was set to AMBER
Added comment: PMID:42378292 describes two unrelated families with ID, language impairment and cognitive dysfunction. One individual harboured a de novo nonsense variant, p.Tyr240*, absent from gnomAD. A second had an inherited p.Gln268Arg missense variant (affected parent), also absent from gnomAD; brain MRI in the proband and parent showed brain anomalies.
Two additional unrelated individuals with developmental delay carried de novo missense variants, p.Arg115His (34 heterozygotes in gnomAD) and p.Arg238Cys (absent from gnomAD).

Functional evidence: A Y240X mouse model showed embryonic lethality in homozygotes, while heterozygotes had ~50% reduction in DCN4 mRNA, impaired synaptic development and significantly reduced learning ability.
Sources: Literature
Mendeliome v2.0 DCT Gene migrated from ENSG00000080166 to ENSG00000080166 (gene set migration)
Mendeliome v0.13895 DCTN1 Zornitza Stark Marked gene: DCTN1 as ready
Mendeliome v0.13895 DCTN1 Zornitza Stark Gene: dctn1 has been classified as Green List (High Evidence).
Mendeliome v0.13895 DCTN1 Zornitza Stark Phenotypes for gene: DCTN1 were changed from to Neuronopathy, distal hereditary motor, type VIIB, MIM# 607641; MONDO:0011879; Perry syndrome, MIM# 168605
Mendeliome v0.13894 DCTN1 Zornitza Stark Publications for gene: DCTN1 were set to
Mendeliome v0.13893 DCTN1 Zornitza Stark Mode of inheritance for gene: DCTN1 was changed from Unknown to MONOALLELIC, autosomal or pseudoautosomal, NOT imprinted
Mendeliome v0.13892 DCTN1 Zornitza Stark edited their review of gene: DCTN1: Changed phenotypes: Neuronopathy, distal hereditary motor, type VIIB, MIM# 607641, MONDO:0011879, Perry syndrome, MIM# 168605
Mendeliome v0.6148 DCT Zornitza Stark Marked gene: DCT as ready
Mendeliome v0.6148 DCT Zornitza Stark Gene: dct has been classified as Green List (High Evidence).
Mendeliome v0.6148 DCT Zornitza Stark Classified gene: DCT as Green List (high evidence)
Mendeliome v0.6148 DCT Zornitza Stark Gene: dct has been classified as Green List (High Evidence).
Mendeliome v0.6147 DCT Zornitza Stark gene: DCT was added
gene: DCT was added to Mendeliome. Sources: Expert list
Mode of inheritance for gene: DCT was set to BIALLELIC, autosomal or pseudoautosomal
Publications for gene: DCT were set to 33100333
Phenotypes for gene: DCT were set to Oculocutaneous albinism, type VIII, MIM# 619165
Review for gene: DCT was set to GREEN
Added comment: Two unrelated families reported. Functional data including mouse model.
Sources: Expert list
Mendeliome v0.0 DCTN1 Zornitza Stark gene: DCTN1 was added
gene: DCTN1 was added to Mendeliome_VCGS. Sources: Expert Review Green,Victorian Clinical Genetics Services
Mode of inheritance for gene: DCTN1 was set to Unknown