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Congenital Myasthenia v1.20 MACF1 Zornitza Stark Marked gene: MACF1 as ready
Congenital Myasthenia v1.20 MACF1 Zornitza Stark Gene: macf1 has been classified as Amber List (Moderate Evidence).
Congenital Myasthenia v1.20 MACF1 Zornitza Stark Classified gene: MACF1 as Amber List (moderate evidence)
Congenital Myasthenia v1.20 MACF1 Zornitza Stark Gene: macf1 has been classified as Amber List (Moderate Evidence).
Congenital Myasthenia v1.19 MACF1 Zornitza Stark gene: MACF1 was added
gene: MACF1 was added to Congenital Myasthenia. Sources: Literature
Mode of inheritance for gene: MACF1 was set to BIALLELIC, autosomal or pseudoautosomal
Publications for gene: MACF1 were set to 37721175; 30842214
Phenotypes for gene: MACF1 were set to Congenital myasthenic syndrome, MONDO:0018940, MACF1-related
Review for gene: MACF1 was set to AMBER
Added comment: 3 individuals reported with bi-allelic variants in this gene and a myasthenic phenotype, two congenital, one adult. Some functional data supports association.
Sources: Literature