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Ataxia v2.138 RFC4 Sangavi Sivagnanasundram Classified gene: RFC4 as Green List (high evidence)
Ataxia v2.138 RFC4 Sangavi Sivagnanasundram Gene: rfc4 has been classified as Green List (High Evidence).
Ataxia v2.137 RFC4 Sangavi Sivagnanasundram gene: RFC4 was added
gene: RFC4 was added to Ataxia. Sources: Literature
Mode of inheritance for gene: RFC4 was set to BIALLELIC, autosomal or pseudoautosomal
Publications for gene: RFC4 were set to 39106866
Phenotypes for gene: RFC4 were set to Morimoto-Ryu-Malicdan neuromuscular syndrome, MONDO:0975848
Review for gene: RFC4 was set to GREEN
Added comment: PMID 39106866 reports four individuals from four unrelated families with biallelic RFC4 variants presenting with a multisystemic disorder that includes cerebellar ataxia, incoordination, muscle weakness, hearing impairment and reduced body weight. Two of the affected individuals also presented with gait ataxia.
Note: one of the reported variants has a high FAF in gnomAD v4.1 for an AR gene (c.996+2dup - FAF 0.0581%).
Sources: Literature