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Dilated Cardiomyopathy v1.64 SLC6A6 Lucy Spencer edited their review of gene: SLC6A6: Changed rating: AMBER
Dilated Cardiomyopathy v1.64 SLC6A6 Lucy Spencer changed review comment from: This gene was reviewed as limited by ClinGen in 2023 however PMID: 41343195 had not yet been published at that time

PMID: 41343195 four families with Leber congenital amaurosis or early-onset retinal dystrophy, all have homozygous variants in SLC6A6- 2 missense, 1 in frame del, 1 nonsense. Thr249Ile, Ala294Thr, Phe404_Glu449del, Trp113Ter. in 1 family the variant segregated with disease as homozygous in 4 affected siblings and heterozygous in unaffected siblings. Some functional evidence available for the 2 missense demonstrating LOF effects. No clear cardiac phenotype was observed in these families.

PMIDs: 31345061, 31903486 reported Ala78Glu and Gly399Val homozygous; to: This gene was reviewed as limited by ClinGen in 2023 however PMID: 41343195 had not yet been published at that time

PMID: 41343195 four families with Leber congenital amaurosis or early-onset retinal dystrophy, all have homozygous variants in SLC6A6- 2 missense, 1 in frame del, 1 nonsense. Thr249Ile, Ala294Thr, Phe404_Glu449del, Trp113Ter. in 1 family the variant segregated with disease as homozygous in 4 affected siblings and heterozygous in unaffected siblings. Some functional evidence available for the 2 missense demonstrating LOF effects. No clear cardiac phenotype was observed in these families- still amber for the cardiac association

PMIDs: 31345061, 31903486 reported Ala78Glu and Gly399Val homozygous
Dilated Cardiomyopathy v1.64 Lucy Spencer Added reviews for gene SLC6A6 from panel Mendeliome
Dilated Cardiomyopathy v1.2 SLC6A6 Zornitza Stark Phenotypes for gene: SLC6A6 were changed from Early retinal degeneration; cardiomyopathy to Hypotaurinaemic retinal degeneration and cardiomyopathy (HTRDC), MIM#145350; Early retinal degeneration; cardiomyopathy
Dilated Cardiomyopathy v1.1 SLC6A6 Zornitza Stark edited their review of gene: SLC6A6: Changed phenotypes: Hypotaurinaemic retinal degeneration and cardiomyopathy (HTRDC), MIM#145350, Early retinal degeneration, cardiomyopathy
Dilated Cardiomyopathy v0.35 SLC6A6 Zornitza Stark Marked gene: SLC6A6 as ready
Dilated Cardiomyopathy v0.35 SLC6A6 Zornitza Stark Gene: slc6a6 has been classified as Amber List (Moderate Evidence).
Dilated Cardiomyopathy v0.35 SLC6A6 Zornitza Stark Classified gene: SLC6A6 as Amber List (moderate evidence)
Dilated Cardiomyopathy v0.35 SLC6A6 Zornitza Stark Gene: slc6a6 has been classified as Amber List (Moderate Evidence).
Dilated Cardiomyopathy v0.34 SLC6A6 Zornitza Stark gene: SLC6A6 was added
gene: SLC6A6 was added to Dilated Cardiomyopathy. Sources: Literature
Mode of inheritance for gene: SLC6A6 was set to BIALLELIC, autosomal or pseudoautosomal
Publications for gene: SLC6A6 were set to 31345061; 31903486; 29886034
Phenotypes for gene: SLC6A6 were set to Early retinal degeneration; cardiomyopathy
Review for gene: SLC6A6 was set to AMBER
Added comment: Different homozygous missense variants in 2 unrelated consanguineous families with early retinal degeneration, some functional studies. Patients in one of the families also had cardiomyopathy. (PMIDs: 31345061, 31903486) One dilated cardiomyopathy patient with a homozygous deletion at a splice site (PMID: 29886034).
Sources: Literature