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Early-onset Parkinson disease v2.45 DAGLB Zornitza Stark gene: DAGLB was added
gene: DAGLB was added to Early-onset Parkinson disease. Sources: Literature
Mode of inheritance for gene: DAGLB was set to BIALLELIC, autosomal or pseudoautosomal
Publications for gene: DAGLB were set to 35715418; 40244389
Review for gene: DAGLB was set to GREEN
Added comment: PMID 35715418 reports 6 individuals from 4 families and PMID 40244389 reports 3 individuals from 3 families, together comprising 9 individuals from 7 unrelated families with biallelic loss-of-function DAGLB variants causing early‑onset Parkinsonism (onset 27‑52 years) characterized by resting tremor, bradykinesia, rigidity, postural instability and good levodopa response. Functional studies (Western blot loss of DAGLB protein, CRISPR‑SaCas9 knock‑down in mouse nigral dopaminergic neurons reducing 2‑AG levels, and rescue of motor deficits by MAGL inhibition) support loss‑of‑function as the disease mechanism.
Sources: Literature
Early-onset Parkinson disease v0.335 SPR Bryony Thompson Marked gene: SPR as ready
Early-onset Parkinson disease v0.335 SPR Bryony Thompson Gene: spr has been classified as Green List (High Evidence).
Early-onset Parkinson disease v0.335 SPR Bryony Thompson Phenotypes for gene: SPR were changed from to Dopa-responsive dystonia due to sepiapterin reductase deficiency MONDO:0012994
Early-onset Parkinson disease v0.334 SPR Bryony Thompson Publications for gene: SPR were set to
Early-onset Parkinson disease v0.333 SPR Bryony Thompson Mode of inheritance for gene: SPR was changed from Unknown to BIALLELIC, autosomal or pseudoautosomal
Early-onset Parkinson disease v0.264 SPR Claire Fryer-Smith reviewed gene: SPR: Rating: AMBER; Mode of pathogenicity: None; Publications: 22522443, 11920285, 14663042, 16443856, 21782285, 32813147; Phenotypes: Dystonia, dopa-responsive, due to sepiapterin reductase deficiency (MIM# 612716); Mode of inheritance: BOTH monoallelic and biallelic, autosomal or pseudoautosomal
Early-onset Parkinson disease v0.0 SPR Zornitza Stark gene: SPR was added
gene: SPR was added to Early onset Parkinson disease_MelbourneGenomics_VCGS. Sources: Expert Review Green,Victorian Clinical Genetics Services,Melbourne Genomics Health Alliance Complex Neurology Flagship
Mode of inheritance for gene: SPR was set to Unknown